Antisense Oligonucleotide Tofersen Distribution in the Central Nervous System of SOD1 -ALS Autopsy Tissue Donors
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DOI: 10.1001/jamaneurol.2026.2195
文献链接: https://jamanetwork.com/journals/jamaneurology/fullarticle/2850993
其他信息:
出版社: American Medical Association (AMA)
作者: Amanda J. Guise; Monica Thanawala Sellon; Shanu F. Roemer; Michael Monine; Nicole T. Comfort Harris; Dan Bartlett; Eric David; Shanqin Xu; Luke Jandreski; Sohail Malek; Steve Garafalo; Ivan Nestorov; Margaret D. Ireland; Andrew King; Robert P. Bowser; Vladislav Korobeynikov; John Ravits; Pamela J. Shaw; J. Robin Highley; Toby A. Ferguson; Stephanie Fradette; Danielle L. Graham; Eric J. Sorenson; Björn Oskarsson; R. Ross Reichard; Dennis W. Dickson; Sabrina Paganoni; Suma Babu; Derek H. Oakley; Matthew P. Frosch; Timothy M. Miller; Robert C. Bucelli; Richard J. Perrin; Cindy V. Ly; Edward D. Plowey

