In vivo base editing gene therapy for heterozygous familial hypercholesterolemia: a phase 1 trial
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DOI: 10.1038/s41591-026-04254-4
文献链接: https://www.nature.com/articles/s41591-026-04254-4
其他信息:
出版社: Springer Science and Business Media LLC
作者: Ping Wan; Siyuan Tang; Dongni Lin; Yuming Lu; Mei Long; Ling Xiao; Yanhong Jiang; Jiaoyang Liao; Xiaoying Ma; Ying Liu; Wensu Yu; Michael Ott; Zi Jun Wang; Yuxuan Wu; Taihua Yang; Qiang Xia
全文下载地址: https://www.nature.com/articles/s41591-026-04254-4.pdf

