Potential of cell-penetrating peptide-conjugated antisense oligonucleotides for the treatment of SMA
用户zCL_XFDWAdZs
1个月前
98
10
已完结
1. 系统已在2026-04-08 16:20:15对应助文件进行删除
2. 如有需要请重新发布求助信息
注: 所有应助的资源仅供学习交流使用, 不得违反相关法律法规
DOI:
文献链接:
其他信息:
J Leckie, T Yokota
Molecules, 2024
mdpi.com
Spinal muscular atrophy (SMA) is a severe neuromuscular disorder that is caused by
mutations in the survival motor neuron 1 (SMN1) gene, hindering the production of functional …

