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RAG-17, a Novel siRNA Therapy for SOD1-ALS: Safety and Preliminary Efficacy from a First-in-human Trial (S5.003)复制

用户aKgJC6g3RnhA 1个月前 71 10 已关闭

DOI: 10.1212/wnl.0000000000212372复制

文献链接: https://www.neurology.org/doi/10.1212/WNL.0000000000212372复制

其他信息:

出版社: Ovid Technologies (Wolters Kluwer Health)
作者: Jinyi Ye; Lingling Jiang; Ling Wang; Yuesong Pan; Xuan Wang; Hui Qu; Xiaoling Liao; Xuejiao Zhou; Shawn Zhang; Moorim Kang; Long-Cheng Li; Weiqi Chen; Yilong Wang

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2026-02-09 16:10:43 [发起求助]