RAG-17, a Novel siRNA Therapy for SOD1-ALS: Safety and Preliminary Efficacy from a First-in-human Trial (S5.003)
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DOI: 10.1212/wnl.0000000000212372
文献链接: https://www.neurology.org/doi/10.1212/WNL.0000000000212372
其他信息:
出版社: Ovid Technologies (Wolters Kluwer Health)
作者: Jinyi Ye; Lingling Jiang; Ling Wang; Yuesong Pan; Xuan Wang; Hui Qu; Xiaoling Liao; Xuejiao Zhou; Shawn Zhang; Moorim Kang; Long-Cheng Li; Weiqi Chen; Yilong Wang

