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The Nonclinical Disposition and Pharmacokinetic/Pharmacodynamic Properties of N-Acetylgalactosamine–Conjugated Small Interfering RNA Are Highly Predictable and Build Confidence in Translation to Human复制

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DOI: 10.1124/dmd.121.000428复制

文献链接: https://linkinghub.elsevier.com/retrieve/pii/S0090955624008067复制

其他信息:

出版社: Elsevier BV
作者: Robin McDougall; Diane Ramsden; Sagar Agarwal; Saket Agarwal; Krishna Aluri; Michael Arciprete; Christopher Brown; Elena Castellanos-Rizaldos; Klaus Charisse; Saeho Chong; Joseph Cichocki; Kevin Fitzgerald; Varun Goel; Yongli Gu; Dale Guenther; Bahru Habtemariam; Vasant Jadhav; Maja Janas; Muthusamy Jayaraman; Jeffrey Kurz; Jing Li; Ju Liu; Xiumin Liu; Steven Liou; Chris Maclauchlin; Martin Maier; Muthiah Manoharan; Jayaprakash K. Nair; Gabriel Robbie; Karyn Schmidt; Peter Smith; Christopher Theile; Akshay Vaishnaw; Scott Waldron; Yuanxin Xu; Xuemei Zhang; Ivan Zlatev; Jing-Tao Wu

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