Neonatal systemic gene therapy restores cardiorespiratory function in a rat model of Pompe disease
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DOI: 10.1016/j.ymthe.2025.06.022
文献链接: https://linkinghub.elsevier.com/retrieve/pii/S1525001625004733
其他信息:
出版社: Elsevier BV
作者: David D. Fuller; Sabhya Rana; Prajwal P. Thakre; Ethan S. Benevides; Megan K. Pope; Adrian G. Todd; Victoria N. Jensen; Lauren Vaught; Denise A. Cloutier; Roberto A. Ribas; Reece C. Larson; Matthew S. Gentry; Ramon C. Sun; Vijay Chandran; Manuela Corti; Darin J. Falk; Barry J. Byrne

