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Nonviral delivery of chemically modified tRNA rescues nonsense mutations in cystic fibrosis复制

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DOI: 10.1126/science.aeb0054复制

文献链接: https://www.science.org/doi/10.1126/science.aeb0054复制

其他信息:

出版社: American Association for the Advancement of Science (AAAS)
作者: Jingan Chen; Muye Zhou; Songtao Dong; Fanglin Gong; Rasangi Tennakoon; Breanna Y. Seto; Ziyan Rachel Chen; Zhichang Peter Zhou; Jingyi Pan; Yue Xu; Sijin Luozhong; Colette Maya Macarios; Santiago Tijaro-Bulla; Tanja Gonska; Jim Hu; Haissi Cui; Bowen Li

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