In Vivo Base Editing of PCSK9 with VERVE-102 for Hypercholesterolemia
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文献链接: http://www.nejm.org/doi/10.1056/NEJMoa2601283
其他信息:
出版社: Massachusetts Medical Society
作者: Scott B. Vafai; Jörg Täubel; Thomas Ashdown; Riyaz S. Patel; Sadaf Diamondali; Jaimini Cegla; Handrean Soran; Bilal Bashir; Alexander Abitbol; Daniel Gaudet; Alex Lauzière; Liam R. Brunham; David E. Newby; Stephen J. Nicholls; Russell S. Scott; Jane Kerr; Jean-Claude Tardif; Catherine Lunken; Steve E. Humphries; Verena Karsten; Patrick D. Tyler; Xinyan Zhang; Nidal Huniti; Patrick A. Flight; Chelsey L. Jensen; Rick Falzone; Joseph C. Biedenkapp; Troy Lister; Leslie E. Stolz; Amit V. Khera; Sekar Kathiresan

