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Safety and efficacy of trehalose in amyotrophic lateral sclerosis (HEALEY ALS Platform Trial): an adaptive, phase 2/3, double-blind, randomised, placebo-controlled trial复制

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DOI: 10.1016/S1474-4422(25)00173-5复制

文献链接: https://linkinghub.elsevier.com/retrieve/pii/S1474442225001735复制

其他信息:

出版社: Elsevier BV
作者: Shafeeq Ladha; Lori Chibnik; Melanie Quintana; Jianing Wang; Eric Macklin; Benjamin Saville; Michelle Detry; Matteo Vestrucci; Giorgio Paulon; Anna McGlothlin; Zachary Simmons; Hristelina Ilieva; Marianne Chase; Lindsay Heyd; Brittney Harkey; Alex Sherman; Jeremy Shefner; James Berry; Suma Babu; Elisa Giacomelli; Hong Yu; Gale Kittle; Meghan Hall; Doreen Ho; Daragh Heitzman; Kevin Felice; Joseph Americo Fernandes; Hani Kushlaf; Omar Jawdat; Laura Rosow; Timothy Miller; Andrea Swenson; Michael Elliott Elliott; Johnathan McKinnon; Jackie Whitesell; Jonathan Katz; Eufrosina Young; Shakti Nayar; Tawfiq Al-Lahham; Senda Ajroud-Driss; Lindsay Zilliox; Alison Walsh; Jim Caress; Laura A Foster; Kelly G Gwathmey; Richard Bedlack; Nicholas J Maragakis; Dominic Fee; Edward J Kasarskis; Margaret Ayo Owegi; Said R Beydoun; Michael D Weiss; I-Hweii Amy Chen; Paul T Twydell; Jeffrey Rosenfeld; David Walk; Amber Erickson; Ximena Arcila-Londono; Elham Bayat; Adam Quick; Michael Baer; Summer Gibson; Robert Dedick Connors; Eduardo Locatelli; Sheetal Shroff; Courtney E McIlduff; Namita A Goyal; Richard Lewis; Michael Rivner; Cynthia Bodkin; Abel Wu; Gustavo Alameda; Luke Pilipski; Warren Wasiewski; Raj Mehra; Merit Cudkowicz; Sabrina Paganoni; Eric Macklin; Lori Chibnik; Douglas Hayden; PoYing Lai; Rachel Donahue; Hao-Wun Chen; Jianing Wang; Melanie Quintana; Benjamin Saville; Michelle Detry; Matteo Vestrucci; Giorgio Paulon; Anna McGlothlin; Doreen Ho; Alexandra McCaffrey; Merit Cudkowicz; Sabrina Paganoni; James Berry; Suma Babu; Jennifer Scalia; Sarah Luppino; Elisa Giacomelli; Erica Scirocco; Daragh Heitzam; Alan Martin; Kevin Felice; Charles Whitaker; Joseph Americo Fernandes; Ezequiel Piccione; Pariwat Thaisetthawatkul; Hani Kushlaf; Robert Neel; Omar Jawdat Jawdat; Constantine Farmakidis Farmakidis; Shafeeq Ladha Ladha; Bill Jacobsen; Jourdan Milliard; Robert Bowser; Jeremy Shefner; Laura Rosow; Catherine Lomen-Hoerth; Timothy Miller; Amber Malcolm; Andrea Swenson; Christopher Nance; Michael Elliott Elliott; David Ivanick; undefined Johnathan; Naya McKinnon; Jackie Whitesell; Brittany Guthrie; Jonathan Katz; Liberty Jenkins; Eufrosina Young; Jenny Meyer; Shakti Nayar; Zachary Simmons; James Grogan; Xiaowei Su; Mansoureh Mamarabadi; Tawfiq Al-Lahham; David Lacomis; Senda Ajroud-Driss; Robert Sufit; April Szymanski; Lindsay Zilliox; Montserrat Diaz-Abad; Alison Walsh; Alissa Romano; Jim Caress; Michael Cartwright; Laura A. Foster; Kelly G. Gwathmey; Qihua Fan; Richard Bedlack; Xiaoyan Li; Sarah Parker; Nicholas J. Maragakis; Lora L. Clawson; Alpa Uchil; Kristen Riley; JinAe Arneklev; Dominic Fee; David Shrilla; Edward J. Kasarskis; Zabeen Mahuwala; Vishakhadatta (Vish) Mathur Kumaraswamy; Margaret Ayo Owegi; Robert H. Brown; Kate Daniello; Said R. Beydoun; Leila Darki; Rodrigo Rodriguez; Michael D Weiss; Nassim Rad; Leo H. Wang; I-Hweii Amy Chen; Niraja Suresh; Jerrica Farias; Tuan Vu; Paul T. Twydell; Jeffrey Rosenfeld; Jasdeep Kaur; David Walk; Sam Maiser; Amber Erickson; Daniel S. Newman; Ximena Arcila-Londono; Kara Steijlen; Elham Bayat; Adam Quick; Stephen Kolb; Sarah Heintzman; Michael Baer; Colin Quinn; Lauren Elman; Summer Gibson; Mark Bromberg; Hristelina Ilieva; Lori Williams; Piera Pasinelli; Robert Dedick Connors; Florian P Thomas; Eduardo Locatelli; Gabriela Lopes; Sheetal Shroff; Ericka P. Greene; Courtney E. McIlduff; Seward Rutkove; Namita A. Goyal; Jeffery Mullen; Richard Lewis; Frank Diaz; Michael Rivner; Benjamin Barnes; Cynthia Bodkin; Abel Wu; Gustavo Alameda; Luisa Arroyave; Abbey Bailey; Jesse Bailey; Victoria Barlow; Allison Bulat; Genevive Changkuon; Marianne Chase; Melissa Cirino; Derek Dagostino; Christina Deignan; Emma Deirmendjian; Annette De Mattos; Sofia DiStefano; Kristin Drake; Michaela Estes; Kenneth Faulconer; Precious Figueroa-Szostek; Tessa Garozzo; Brittney Harkey; Meredith Hasenoehrl; Jennifer Henrique; Natalie Henrique; Samuel Hurwitz; Courtney Igne; Liam Irwin; Katie Jentoft; Boglarka Jordan; Igor Katsovskiy; Olga Kharakozova; Taylor Kolvek; Alexander Korin; Thuong La; Haining Li; Ilya Novak; Joe Ostrow; Jaclyn Pagliaro; Jack Palillo; Payal Patel; Janae Patterson; Minh Phan; Najla Popel; Lindsay Heyd; Serena Proueng; Jesse Rosenthal; Alex Sherman; Catherine Small; Natalia Tarasenko; Mirna Thomas; Eric Tustison; Prasha Vigneswaran; Yusra Wahab; Isaac Whitworth; Spencer Wright; Hong Yu; Mariah Connolly; Diana De Santiago; Adrian Felix; Karly Garrett; Meghan Hall; Jenny Hamilton; Kamran Khan; Gale Kittle; Marlee Lovett; Linda Nelson; Marissa Pabon; Diana Rede; Ahmed Fetouh; Cornelia Kamp; Julie Kennedy; Joan Woodcook; Arian Horbovetz; Andrew McGarry; Margherita Torti

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