An Antibody–Oligonucleotide Conjugate for Myotonic Dystrophy Type 1
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DOI: DOI: 10.1056/NEJMoa2407326
文献链接: http://www.nejm.org/doi/10.1056/NEJMoa2407326
其他信息:
出版社: Massachusetts Medical Society
作者: Nicholas E. Johnson; Li-Jung Tai; Johanna I. Hamel; John W. Day; Jeffrey M. Statland; Payam Soltanzadeh; Sankarasubramoney H. Subramony; Charles A. Thornton; W. David Arnold; Matthew Wicklund; Miriam L. Freimer; Kate Eichinger; Jeanne Dekdebrun; Chao-Yin Chen; Varun Goel; Bradley McEvoy; Yiming Zhu; Steven G. Hughes; Elizabeth J. Ackermann; Arthur A. Levin

