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Efficacy and safety of cemdisiran siRNA in myasthenia gravis (NIMBLE): a double-blind, randomised, placebo-controlled, phase 3 trial复制

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DOI: 10.1016/s0140-6736(26)00690-2复制

文献链接: https://linkinghub.elsevier.com/retrieve/pii/S0140673626006902复制

其他信息:

出版社: Elsevier BV
作者: Tuan Vu; Ali A Habib; Saiju Jacob; Renato Mantegazza; Hiroyuki Murai; John Vissing; Aziz Shaibani; Todd Levine; Yessar Hussain; Andreas Meisel; Agnieszka Adamczak-Ratajczak; Jan Ilkowski; Paulo Sgobbi; Alexandre Guerreiro; Sushan Luo; Rodrigo Pavani; Umesh Chaudhari; Neda Jalali; Michelle DeVeaux; Warren Moore; Karoline A Meagher; Michael E Burczynski; Shital Kokate; Steven Sherman; Dipti Pawaskar; Nikhil Singh; Amal Souttou; Andres Sirulnik; Lorah Perlee; George D Yancopoulos; James F Howard; Jan De Bleecker; Sergio Semeraro Jordy; Alexandre Guerreiro; Ana Marina Silva; Paulo Victor Sgobbi de Souza; Edmar Zanoteli; Zaeem Siddiqi; Chongbo Zhao; Huan Yang; Hui Deng; Zhangyu Zou; Qilong Jiang; Yuzhou Guan; Haishan Jiang; Fei Xu; Wenshuang Zeng; Yuanqi Zhao; Zuneng Lu; Fudong Shi; Shixiong Huang; Jiann-Horng Yeh; Long-Sun Ro; Yuh-Cherng Guo; Nai-Wen Tsai; Yuan-Ting Sun; John Vissing; Henning Andersen; Jakob Holbech; Izabella Obal; Sophie Demeret; Saskia Bresch; Alexander Tsiskaridze; Ia Rukhadze; Temur Margania; Ketevan Ugulava; Benedikt Schoser; Andreas Meisel; Tim Hagenacker; Rahul Kulkarni; Arvind Prabhu; Manish Modi; Vishnu Vy; U. Aruna Kumari; Rukmini Kandadai; Praveen Kumar Srikanteshwar; Sireesha Yareeda; Neeraj Jain; Suresh Kumar; Stefania Morino; Renato Mantegazza; Lorenzo Maggi; Michelangelo Maestri Tassoni; Maurizio Inghilleri; Giovanni Fabbrini; Antonio Suppa; Manlio Sgarzi; Manabu Inoue; Naomi Kanzato; Takashi Tokashiki; Akiyuki Uzawa; Hideto Nakajima; Michi Kawamoto; Masayuki Masuda; Andrzej Szczudlik; Anna Kostera-Pruszczyk; Malgorzata Bilinska; Agnieszka Adamczak-Ratajczak; Mariusz Grudniak; Jan Ilkowski; Elena Cortés Vicente; Teresa Sevilla Mantecón; Ihsan Şükrü Şengün; Murat Terzi; Saiju Jacob; Channa Hewamadduma; Marc Feinberg; Aziz Shaibani; Yessar Hussain; Said Beydoun; George Li; William Justiz; Todd Levine; Jacob Rube; Ali A. Habib; Sami Khella; Andrew Gordon; Tuan Vu; Raghav Govindarajan; Sashikumar Tharmarajah

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2026-04-27 20:24:22 [发起求助]